Companies in #Muscular Dystrophy

Found 1 company operating in this sector.

Epicrispr Biotechnologies

Private

Epigenetic therapies for facioscapulohumeral muscular dystrophy (FSHD). Lead program EPI-321 targets the genetic root cause. Also researching alpha-1 antitrypsin deficiency and familial hypercholesterolemia.

Sector:Gene Therapy / Epigenetics

HQ:Cambridge, Massachusetts, USA

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