Companies in #Gene Editing
Found 2 companies operating in this sector.
CRISPR Therapeutics is a Swiss-American biopharmaceutical company pioneering CRISPR/Cas9 gene editing therapies for serious diseases. The company developed Casgevy (exagamglogene autotemcel), the first CRISPR-based gene therapy approved by the FDA and EMA for sickle cell disease and transfusion-dependent beta thalassemia. The company is advancing a broad pipeline spanning hemoglobinopathies, oncology, autoimmune diseases, and in vivo gene editing programs.
Prime Medicine is a clinical-stage biotechnology company pioneering prime editing, a next-generation gene editing technology that can make precise edits to DNA without double-strand breaks. Its pipeline targets liver, ocular, and CNS genetic diseases.