Companies in #Charcot-Marie-Tooth Disease
Found 1 company operating in this sector.
Actio Biosciences
PrivateGenetics-driven precision medicine company developing small molecule therapeutics for rare and common diseases. Pipeline includes KCNT1 inhibitor for epilepsy and TRPV4 inhibitor for Charcot-Marie-Tooth disease. Acquired by Jazz Pharmaceuticals for $820M.