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Companies in #Charcot-Marie-Tooth Disease

Found 1 company operating in this sector.

Genetics-driven precision medicine company developing small molecule therapeutics for rare and common diseases. Pipeline includes KCNT1 inhibitor for epilepsy and TRPV4 inhibitor for Charcot-Marie-Tooth disease. Acquired by Jazz Pharmaceuticals for $820M.

Sector:Rare Disease / Precision Medicine
HQ:San Diego, California, USA