Companies in #ALS
Found 2 companies operating in this sector.
Cytokinetics is a late-stage biopharmaceutical company focused on discovering and developing muscle biology-directed therapies for diseases of impaired muscle function, including cardiac myosin modulators for heart failure and skeletal muscle activators for ALS and SMA.
Denali Therapeutics (NASDAQ: DNLI) is a biotechnology company headquartered in South San Francisco, California, developing a broad portfolio of therapeutics for neurodegenerative diseases through its proprietary blood-brain barrier (BBB) delivery platform (the ATV/Otv platform, including Enzyme Transport Vehicle and Oligonucleotide Transport Vehicle technologies). Denali's clinical and preclinical pipeline targets Parkinson's disease (BIIB122/DNL151, partnered with Biogen), Hunter syndrome (DNL310, tividenofusp alfa), ALS (DNL343), and multiple other lysosomal storage diseases and neurodegenerative indications. The company was founded in 2015 by a team that included former Genentech scientists.