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Scholar Rock

NASDAQ: SRRK $48.98 USD~$3.5B MCAP

Scholar Rock is a clinical-stage biopharmaceutical company focused on the discovery and development of innovative medicines for the treatment of serious diseases in which signaling by protein growth factors plays a fundamental role. Its lead product, apitegromab, is being developed for spinal muscular atrophy (SMA).

Company Info

Sector:Biopharmaceuticals
Headquarters:Cambridge, Massachusetts, United States
Founded:2012

Upcoming Milestones & Key Dates

Late 2026
Regulatory

Apitegromab BLA submission decision

Q4 2026
Clinical

SRK-439 Phase 1 initial data

Clinical Development Pipeline

Apitegromab

Target: Latent myostatin
Spinal muscular atrophy (SMA)
Preclinical
Phase 1
Phase 2
Phase 3
Approved

SRK-439

Target: GDF11/GDF8
Obesity / metabolic disease
Preclinical
Phase 1
Phase 2
Phase 3
Approved

SRK-181

Target: Latent TGFβ1
Immuno-oncology combinations
Preclinical
Phase 1
Phase 2
Phase 3
Approved

Recent News

Leadership Team

David L. Hallal

Chief Executive Officer

Mo Qatanani

Chief Scientific Officer

Tracy Wong

Chief Financial Officer

Careers & Job Openings

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