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Sarepta Therapeutics

NASDAQ: SRPT $15.68 USD~$10B MCAP

Sarepta Therapeutics is a commercial-stage biopharmaceutical company focused on precision genetic medicines for rare neuromuscular and central nervous system diseases.

Company Info

Sector:Biopharmaceutical
Headquarters:Cambridge, Massachusetts, United States
Founded:1980

Upcoming Milestones & Key Dates

2027-Q1
Clinical

Elevidys label expansion data

Clinical Development Pipeline

Elevidys

Target: Micro-dystrophin
Duchenne muscular dystrophy
Preclinical
Phase 1
Phase 2
Phase 3
Approved

SRP-9001

Target: Gene therapy
Limb-girdle muscular dystrophy
Preclinical
Phase 1
Phase 2
Phase 3
Approved

SRP-5051

Target: Exon 51 skipping
Duchenne muscular dystrophy
Preclinical
Phase 1
Phase 2
Phase 3
Approved

Recent News

Leadership Team

Doug Ingram

President and Chief Executive Officer

Louise Rodino-Klapac

Chief Scientific Officer

Ian Estepan

Chief Financial Officer

Careers & Job Openings

See all open roles

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